Cardiovascular

Endothelial and platelet dysfunction in systemic sclerosis with pulmonary hypertension.

TL;DR

SSc patients have endothelial dysfunction and increased platelet activity, which exhibits correlation with TRVmax, and TRAP-6-induced platelet aggregation and FMD were independently associated with TRVmax in multivariable regression analysis.

Key Findings

Flow-mediated dilation (FMD) was progressively lower in SSc patients compared to controls, decreasing with increasing pulmonary hypertension probability.

  • FMD was 13.3 ± 3.9% in age-matched controls
  • FMD decreased to 5.6 ± 1.7% in SSc patients with low PH probability
  • FMD further decreased to 4.6 ± 0.4% in SSc patients with intermediate PH probability
  • FMD was lowest at 3.8 ± 0.4% in SSc patients with confirmed PH
  • Endothelial function was assessed by flow-mediated dilation of the brachial artery

SSc patients with confirmed pulmonary hypertension had higher blood nitrite levels than controls or patients with low PH probability.

  • Blood nitrite levels were measured by chemiluminescence method
  • Elevated nitrite in confirmed PH patients compared to both controls and low PH probability SSc patients
  • Blood nitrite serves as a marker of endothelial nitric oxide production and endothelial function
  • This elevation in confirmed PH patients was in contrast to the pattern of reduced FMD

Maximal tricuspid regurgitant velocity (TRVmax) correlated inversely with FMD and positively with platelet aggregation.

  • TRVmax is an echocardiographic parameter used to assess PH probability
  • The inverse correlation with FMD indicates that worse endothelial function is associated with higher TRVmax
  • The positive correlation with platelet aggregation indicates that greater platelet activity is associated with higher TRVmax
  • Platelet activity was measured by light transmission aggregometry in response to ADP and TRAP-6 stimulation

TRAP-6-induced platelet aggregation and FMD were independently associated with TRVmax in multivariable regression analysis.

  • Multivariable regression analysis was performed to assess independent associations with TRVmax
  • TRAP-6 (thrombin receptor-activating peptide-6) was used as a platelet stimulant in light transmission aggregometry
  • Both platelet aggregation (TRAP-6-induced) and FMD remained independently associated with TRVmax after adjustment for other variables
  • This suggests both endothelial dysfunction and increased platelet activity independently contribute to pulmonary vascular changes in SSc

Nebulized sodium nitrite transiently reduced TRVmax in two SSc patients with pulmonary hypertension.

  • This was a proof-of-concept observation in two patients
  • Sodium nitrite was administered via nebulization
  • The reduction in TRVmax was transient
  • This finding suggests a potential therapeutic role for inhaled nitrite in SSc-associated pulmonary hypertension

PH diagnosis in SSc patients was confirmed by right heart catheterization, with probability assessed by echocardiography.

  • Patients were stratified into low PH probability, intermediate PH probability, and confirmed PH groups
  • Echocardiographic parameters including TRVmax were used to assess PH probability
  • Right heart catheterization was the gold standard for confirming PH diagnosis
  • Systemic sclerosis is described as an autoimmune connective tissue disease characterized by vasculopathy, inflammation, and fibrosis

What This Means

This research suggests that patients with systemic sclerosis (SSc), an autoimmune disease affecting connective tissue, experience progressive deterioration of blood vessel function and increased platelet activity (blood cell clotting tendency) as pulmonary hypertension (high blood pressure in the lungs) develops and worsens. The study measured how well the brachial artery in the arm could widen in response to increased blood flow (a test called flow-mediated dilation, or FMD) and found that SSc patients had significantly impaired vessel function compared to healthy controls, with the most severe impairment seen in those with confirmed pulmonary hypertension. Additionally, the speed at which blood leaks back through the tricuspid heart valve — an indicator of pulmonary pressure — was inversely related to vessel function and directly related to platelet stickiness. Using statistical modeling, the researchers found that both poor endothelial (vessel lining) function and elevated platelet aggregation independently predicted higher pulmonary pressures, suggesting these two processes may each contribute separately to disease progression. In a small observation of two patients, inhaling a solution of sodium nitrite — a compound that can release nitric oxide, which relaxes blood vessels — temporarily lowered pulmonary pressures as measured by echocardiography. This research suggests that monitoring endothelial function and platelet activity in SSc patients could help identify those at greatest risk of developing severe pulmonary hypertension. It also raises the possibility that therapies targeting these pathways, such as inhaled nitrite compounds, might offer benefit in SSc-associated pulmonary hypertension, though larger studies would be needed to confirm this.

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Citation

Imerbtham T, Sriwantana T, Ngamjanyaporn P, Sotananusak T, Ngammisri P, Trerayapiwat K, et al.. (2026). Endothelial and platelet dysfunction in systemic sclerosis with pulmonary hypertension.. PloS one. https://doi.org/10.1371/journal.pone.0357987